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PCSK9

PCSK9 — the molecular target that 1 compounds in the wiki act on.

In one line: A protein that destroys your "bad-cholesterol vacuum cleaners" — blocking it slashes LDL.

Your liver has receptors that act like vacuum cleaners, pulling bad (LDL) cholesterol out of your blood. PCSK9 is a protein that destroys those vacuums. Newer heart drugs block PCSK9 so the vacuums survive longer and clear far more LDL — dropping it dramatically. One version (inclisiran) silences PCSK9 with an injection needed only twice a year.

It's one of the most powerful cholesterol-lowering tools ever made, used when statins aren't enough.

Compounds acting on PCSK9