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Clofarabine

  • Prescription medicine
  • Given by a clinician
  • Identity checked
  • Sources last checked 2026-09-04

This page shows what was measured, who it was measured in, and what that does not settle.

What Clofarabine does in the body

Pediatric patients 1 to 21 years old with relapsed or refractory acute lymphoblastic leukemia after at least two prior regimens

From the FDA-approved label: Clofarabine is sequentially metabolized intracellularly to the 5’-monophosphate metabolite by deoxycytidine kinase and mono- and di-phospho-kinases to the active 5’-triphosphate metabolite. Clofarabine has affinity for the activating phosphorylating enzyme, deoxycytidine kinase, equal to or greater than that of the natural substrate, deoxycytidine. Clofarabine inhibits DNA synthesis by decreasing cellular deoxynucleotide triphosphate pools through an inhibitory action on ribonucleotide reductase, and by terminating DNA chain elongation and inhibiting repair through incorporation into the DNA chain by competitive inhibition of DNA polymerases.

What happened in people

RNAWiki has not yet published a reviewed conclusion for this use.

A fixed RNAWiki sentence

Where this came from

Wording RNAWiki always uses, not a finding about this substance.

No reviewed claim names a result for any goal on this record.

No source is stored against this line.

The limit that matters most

Not recorded.

Where it acts
Not recorded.
Kind of result
No result is published, so no kind of result applies yet
Supervision
Professional supervision is normally required. A regulator classifies this substance in a way that restricts how it is supplied.

What the registries record it as

  • The substance registry classes this as chemical.

    FDA substance registry · 762RDY0Y2H · read 2026-08-29

  • Its recorded molecular formula is C10H11ClFN5O3, weighing 303.68 Daltons.

    US prescribing information · 54436453-882e-406b-87a3-049d150101c6 · read 2026-08-30

Where each sentence above came from

No recorded sentence describes the change this makes in a way that stands on its own. The page opens with what it is taken for instead, and the recorded explanation follows below.

Shown as the opening line on this page.

No statement of the main limit is recorded.

The four opening statements run to 119 words.

Words this page uses

Four words worth knowing first

Chosen from what this page shows, with each one explained before the word it depends on.

Biomarker

A biomarker is a number from a test that stands in for something about health.

A picture of it, and where the picture fails

A biomarker is like a fuel gauge.

Where that stops being true. A gauge is wired to the tank. Many biomarkers are only loosely tied to health.

What people get wrong. A better number is read as a better life. Several medicines improved a number and helped nobody.

A measurable indicator used as a substitute for a clinical outcome of interest.

Placebo

A placebo is a dummy treatment given so the real one can be compared with it.

A picture of it, and where the picture fails

A placebo is like a blank control in an experiment.

Where that stops being true. A blank does nothing. People given a placebo often do get better.

What people get wrong. A placebo effect is read as imaginary. The improvement is measured and real.

An inactive intervention matched in appearance to the test intervention, used to control for non-specific effects.

Comparator

A comparator is whatever the treatment was measured against.

A picture of it, and where the picture fails

It is like the other runner in a race.

Where that stops being true. A race has one winner. A study can show both arms improved.

What people get wrong. Results are read without asking what the other group got. Beating nothing is not beating a treatment.

The control condition against which the experimental intervention is assessed.

What happened in peopleRead from sources, not yet reviewed

What happened in people

Each card is one study: the exact question it asked, who was in it, and whether it showed what it set out to show.

DFS of Non-DS HR Post-induction Patients Receiving Intrathecal (IT) Methotrexate (MTX) Compared With Patients Receiving Intrathecal Triple Therapy (ITT) on a Modified Berlin-Frankfurt-Munster (MBFM) Interim Maintenance High-dose Methotrexate Backbone

The study did not show it

Who was studied
NCT02883049
How many people
5949
Study design
Phase 3
Compared against
Not recorded for this study
Kind of result
A number that stands in for health
What was found
Result not recorded on this page
Repeated elsewhere
Unreplicated

What this does not prove. A study that did not show an effect does not show that no effect exists anywhere.

The limits of this study, and where it came from

Main limit. No limitation is recorded for this study.

How far it carries. This study is recorded from the curated record, not from the registry match.

Form and route. Intravenous

Interval reported. Not recorded in this summary

Written into the record, not signed off as a reviewed claim.

  • openFDA Drugs@FDA · a recorded source, not a stored snapshot
  • openFDA NDC Directory · a recorded source, not a stored snapshot
  • openFDA SPL label · a recorded source, not a stored snapshot
  • PubChem PUG-REST · a recorded source, not a stored snapshot

Overall survival

The study did not show it

Who was studied
NCT00454480
How many people
2000
Study design
Phase 2/Phase 3
Compared against
Not recorded for this study
Kind of result
Living longer, or avoiding a major event
What was found
Result not recorded on this page
Repeated elsewhere
Unreplicated

What this does not prove. A study that did not show an effect does not show that no effect exists anywhere.

The limits of this study, and where it came from

Main limit. No limitation is recorded for this study.

How far it carries. This study is recorded from the curated record, not from the registry match.

Form and route. Intravenous

Interval reported. Not recorded in this summary

Written into the record, not signed off as a reviewed claim.

  • openFDA Drugs@FDA · a recorded source, not a stored snapshot
  • openFDA NDC Directory · a recorded source, not a stored snapshot
  • openFDA SPL label · a recorded source, not a stored snapshot
  • PubChem PUG-REST · a recorded source, not a stored snapshot

Event-free survival of ALL patients (EFS)

The study did not show it

Who was studied
NCT03117751
How many people
790
Study design
Phase 2/Phase 3
Compared against
Not recorded for this study
Kind of result
Living longer, or avoiding a major event
What was found
Result not recorded on this page
Repeated elsewhere
Unreplicated

What this does not prove. A study that did not show an effect does not show that no effect exists anywhere.

The limits of this study, and where it came from

Main limit. No limitation is recorded for this study.

How far it carries. This study is recorded from the curated record, not from the registry match.

Form and route. Intravenous

Interval reported. Not recorded in this summary

Written into the record, not signed off as a reviewed claim.

  • openFDA Drugs@FDA · a recorded source, not a stored snapshot
  • openFDA NDC Directory · a recorded source, not a stored snapshot
  • openFDA SPL label · a recorded source, not a stored snapshot
  • PubChem PUG-REST · a recorded source, not a stored snapshot

Safety and efficacy of clofarabine combined with pegaspargase (phase II)

The study did not show it

Who was studied
NCT01228331
How many people
745
Study design
Phase 2/Phase 3
Compared against
Not recorded for this study
Kind of result
A number that stands in for health
What was found
Result not recorded on this page
Repeated elsewhere
Unreplicated

What this does not prove. A study that did not show an effect does not show that no effect exists anywhere.

The limits of this study, and where it came from

Main limit. No limitation is recorded for this study.

How far it carries. This study is recorded from the curated record, not from the registry match.

Form and route. Intravenous

Interval reported. Not recorded in this summary

Written into the record, not signed off as a reviewed claim.

  • openFDA Drugs@FDA · a recorded source, not a stored snapshot
  • openFDA NDC Directory · a recorded source, not a stored snapshot
  • openFDA SPL label · a recorded source, not a stored snapshot
  • PubChem PUG-REST · a recorded source, not a stored snapshot

DFS (disease free survival) following first remission achievement (CR : Complete Remission or CRp : Complete Remission but platelet count < 100 x109/L) in younger patients with intermediate-risk or unfavorable-risk AML.

The study did not show it

Who was studied
NCT00932412
How many people
735
Study design
Phase 2
Compared against
Not recorded for this study
Kind of result
Living longer, or avoiding a major event
What was found
Result not recorded on this page
Repeated elsewhere
Unreplicated

What this does not prove. A study that did not show an effect does not show that no effect exists anywhere.

The limits of this study, and where it came from

Main limit. No limitation is recorded for this study.

How far it carries. This study is recorded from the curated record, not from the registry match.

Form and route. Intravenous

Interval reported. Not recorded in this summary

Written into the record, not signed off as a reviewed claim.

  • openFDA Drugs@FDA · a recorded source, not a stored snapshot
  • openFDA NDC Directory · a recorded source, not a stored snapshot
  • openFDA SPL label · a recorded source, not a stored snapshot
  • PubChem PUG-REST · a recorded source, not a stored snapshot

Overall Survival

The study did not show it

Who was studied
NCT02085408
How many people
727
Study design
Phase 3
Compared against
Not recorded for this study
Kind of result
Living longer, or avoiding a major event
What was found
Result not recorded on this page
Repeated elsewhere
Unreplicated

What this does not prove. A study that did not show an effect does not show that no effect exists anywhere.

The limits of this study, and where it came from

Main limit. No limitation is recorded for this study.

How far it carries. This study is recorded from the curated record, not from the registry match.

Form and route. Intravenous

Interval reported. Not recorded in this summary

Written into the record, not signed off as a reviewed claim.

  • openFDA Drugs@FDA · a recorded source, not a stored snapshot
  • openFDA NDC Directory · a recorded source, not a stored snapshot
  • openFDA SPL label · a recorded source, not a stored snapshot
  • PubChem PUG-REST · a recorded source, not a stored snapshot
What we know
RNAWiki holds 6 written-up human studies for this substance, each with the question it asked.
How we know it
Each card names the study, the number of people and what the study set out to measure.
What this does not prove
These summaries were written by a person and have not been signed off as reviewed claims.
Why it matters
A study that failed is as informative as one that worked, and both are here.
What we still do not know
No reviewed claim exists, so no exact population, effect size or interval is published yet.

What is missing or unclearRead from sources, not yet reviewed

Were people like you studied?

RNAWiki cannot tell whether a study fits you. It can show who was in it, and where the result stops carrying.

Who was studied

People similar to this profile were included.

  • Clofarabine Injection is indicated for the treatment of pediatric patients 1 to 21 years old with relapsed or refractory acute lymphoblastic leukemia after at least two prior regimens. This indication is based upon response rate. There are no trials verifying an improvement in disease-related symptoms or increased survival with Clofarabine Injection.

Who is missing from the studies

  • Which groups were under-represented in the studies has not been recorded for this substance. Pregnancy, breastfeeding, children, older adults, and people with liver or kidney conditions are commonly excluded from trials; nothing here says whether they were.

What the label states about particular groups

  • On pediatric, the label states: “Safety and effectiveness have been established in pediatric patients 1 to 21 years old with relapsed or refractory acute lymphoblastic leukemia.”

    US prescribing information · 54436453-882e-406b-87a3-049d150101c6 · read 2026-08-30

  • On older people, the label states: “Safety and effectiveness of clofarabine has not been established in geriatric patients aged 65 and older.”

    US prescribing information · 54436453-882e-406b-87a3-049d150101c6 · read 2026-08-30

  • On people who are pregnant, the label states: “Risk Summary In animal reproduction studies, intravenous administration of clofarabine to pregnant rats and rabbits during organogenesis at doses approximately 0.2- to 1-times the maximum recommended human dose of 52 mg/m 2 based on body surface area (BSA) resulted in embryo-fetal mortality, alterations to growth, and structural abnormalities (see Data ) .”

    US prescribing information · 54436453-882e-406b-87a3-049d150101c6 · read 2026-08-30

  • On people who are breastfeeding, the label states: “Risk Summary There are no data on the presence of clofarabine in human milk, the effects on the breastfed child, or the effects on milk production.”

    US prescribing information · 54436453-882e-406b-87a3-049d150101c6 · read 2026-08-30

  • On people with reduced kidney function, the label states: “Reduce the clofarabine starting dose by 50% in patients with CrCL of 30 to 60 mL/min.”

    US prescribing information · 54436453-882e-406b-87a3-049d150101c6 · read 2026-08-30

Where the result stopped carrying

  • This is a scope explorer, not a diagnosis engine.
  • It shows who was studied so you can see whether people similar to you were included.

RNAWiki cannot tell whether a study fits you. It can show who was in it.

What it would be like to takeRead from sources, not yet reviewed

Why it might seem to do nothing

A real effect and a noticed effect are different things. These are the recorded reasons the two come apart.

It was studied in different people

The people in the studies were not much like the reader.

On this record: Which groups were under-represented in the studies has not been recorded for this substance. Pregnancy, breastfeeding, children, older adults, and people with liver or kidney conditions are commonly excluded from trials; nothing here says whether they were.

The evidence may simply be wrong

Small early studies often do not hold up.

On this record: RNAWiki has not yet published a reviewed conclusion for this use.

Other reasons RNAWiki checked and found nothing for (11)
It was studied for a different goal
The studies measured something else entirely. Nothing in this record points to this reason.
A different form was studied
The studied form is not the form on the shelf. Nothing in this record points to this reason.
There was nothing to correct
Where a level is already normal, topping it up may change nothing. Nothing in this record points to this reason.
Something else had to happen too
In the studies it was paired with training, a diet or another treatment. Nothing in this record points to this reason.
The change is too small to feel
A real change can still sit below what a person notices. Nothing in this record points to this reason.
Day-to-day swing hides it
Sleep, food, stress and time of day move most numbers more than this would. Nothing in this record points to this reason.
Not enough time yet
The studies ran longer than the person has waited. Nothing in this record points to this reason.
It was not taken as studied
Missed days change the result, and studies count them. Nothing in this record points to this reason.
Something else changed at the same time
Two changes at once cannot be told apart afterwards. Nothing in this record points to this reason.
The product may not be what it says
Contents of a sold product are not always what the label states. Nothing in this record points to this reason.
No recorded reason
RNAWiki has nothing stored that would explain it. Nothing in this record points to this reason.

None of these is a reason to take more. Taking more is not a step this page ever suggests.

What it would be like to takeRead from sources, not yet reviewed

What taking it involves

The recorded facts about getting hold of it and using it. Nothing here is a suggestion about what you should do.

How it is supplied

Given by a clinician

Quoted from a source

Where this came from

Copied from a source RNAWiki stored, with the source named.

Read from the recorded approval status.

No source is stored against this line.

Form and route

Intravenous

Source-linked record

Where this came from

A person wrote this into the record with the study named beside it. No reviewer has signed it off.

The form and route recorded on this substance.

No source is stored against this line.

Who oversees it

Professional supervision is normally required. A regulator classifies this substance in a way that restricts how it is supplied.

Quoted from a source

Where this came from

Copied from a source RNAWiki stored, with the source named.

Suppression classes recorded: S1, S3, S4.

No source is stored against this line.

What is in the pack

Sold as solution, injectable, injection, given by the intravenous, injection route.

Source-linked record

Where this came from

A person wrote this into the record with the study named beside it. No reviewer has signed it off.

Recorded notes on how this is sold and what that means for what is in the pack.

No source is stored against this line.

Where it is registered

Regulatory records are listed in the technical disclosure at the foot of this page.

Counted from records

Where this came from

A count of rows RNAWiki holds. It describes our records, not your body.

Register entries are stored per jurisdiction and shown with their dates.

No source is stored against this line.

Why people stop

Not recorded.

Nothing recorded

Where this came from

RNAWiki holds nothing here and says so rather than guessing.

No record of why people stopped taking it is stored for this substance.

No source is stored against this line.

What it would be like to takeNothing found in the sources checked

What can go wrong

Sorted by where each line came from. A regulator's label and a report somebody sent in are not the same kind of fact.

Nothing found in the sources checked

No harm is recorded against this substance in the sources RNAWiki checked. Finding nothing is not the same as showing there is nothing.

The sources listed were searched and held nothing. That is not the same as nothing existing.

Over a long time. No completed tested study window is recorded, so long-term effects are not established by the registry record.

Groups the studies covered thinly. Which groups were under-represented in the studies has not been recorded for this substance. Pregnancy, breastfeeding, children, older adults, and people with liver or kidney conditions are commonly excluded from trials; nothing here says whether they were.

What is missing or unclearRead from sources, not yet reviewed

Does the exact form matter?

Evidence belongs to the exact thing that was tested. A different salt, a different mixture or a different preparation is a different question.

The form that was studied

Intravenous

Source-linked record

Where this came from

A person wrote this into the record with the study named beside it. No reviewer has signed it off.

The form used in the studies cited on this page.

No source is stored against this line.

What is sold

Not recorded.

Nothing recorded

Where this came from

RNAWiki holds nothing here and says so rather than guessing.

Nothing further is recorded about which forms are sold.

No source is stored against this line.

What is recorded as being sold

  • 16 products list this as an active ingredient in the United States drug directory. 16 of them contain it and nothing else.

    FDA National Drug Code directory · 62756-030 · read 2026-08-29

  • They are sold as injection and powder, taken intravenous.

    FDA National Drug Code directory · 62756-030 · read 2026-08-29

  • The regulator's established pharmacologic class for it is nucleic acid synthesis inhibitors [moa] and nucleoside metabolic inhibitor [epc].

    FDA National Drug Code directory · 62756-030 · read 2026-08-29

  • 8 published labels name it as an active ingredient. 8 of them describe this substance alone, which is where its own label text on this page comes from.

    US prescribing information · 54436453-882e-406b-87a3-049d150101c6 · read 2026-08-29

  • Those labels are classed as human prescription drug.

    US prescribing information · 54436453-882e-406b-87a3-049d150101c6 · read 2026-08-29

  • Clofarabine is intravenous at 3 DOSAGE FORMS AND STRENGTHS Injection: 20 mg per 20 mL (1 mg per mL) clear solution in single-dose vial Injection: 20 mg per 20 mL (1 mg per mL) single-dose vial., recorded as fda label in effect 2022-12-12 in the United States.

    US prescribing information · 54436453-882e-406b-87a3-049d150101c6 · read 2026-08-30

Evidence carries across two names for one substance. It does not carry across a salt, a mirror form or a mixture.

What it would be like to takeRead from sources, not yet reviewed

What you could measure

This one is decided with a clinician, so this section holds questions to ask rather than a plan to run.

Self-experiment planning is not offered for a prescription or clinician-supervised medicine. The questions below are for a clinician or pharmacist.

Questions worth asking

  • Which of the trials of Clofarabine studied people like me?
  • What was measured, and for how long?
  • Was the result a laboratory value or a health outcome?
  • What would we watch for, and when would we stop?

Tracking can show whether something changed for you. It cannot show what caused it.

RNAWiki records evidence. It does not say whether this substance is right for you.

What is missing or unclearRead from sources, not yet reviewed

What nobody knows yet

Open questions, each with why it is open and what would close it.

Missing populations

Which groups were under-represented in the studies has not been recorded.

Why it matters. Recorded by the evidence model as a gap on this record.

What would answer it

A study that measures it, and a reviewer to sign it off.

Last checked 2026-09-04. Searched: The sources listed in the receipts at the foot of this page.

Missing long-term data

No completed tested study window is recorded.

Why it matters. Recorded by the evidence model as a gap on this record.

What would answer it

A study that measures it, and a reviewer to sign it off.

Last checked 2026-09-04. Searched: The sources listed in the receipts at the foot of this page.

No reviewed conclusion

RNAWiki has not yet published a reviewed conclusion for this use.

Why it matters. Recorded by the evidence model as a gap on this record.

What would answer it

A study that measures it, and a reviewer to sign it off.

Last checked 2026-09-04. Searched: The sources listed in the receipts at the foot of this page.

Missing interaction studies

No interaction was found in the registers checked. Not finding one is not the same as showing there is none.

Why it matters. Recorded by the evidence model as a gap on this record.

What would answer it

A study that measures it, and a reviewer to sign it off.

Last checked 2026-09-04. Searched: The sources listed in the receipts at the foot of this page.

Formulation uncertainty

Several salts, forms or products of Clofarabine are recorded. Results from one form may not transfer to another.

Why it matters. Recorded by the evidence model as a gap on this record.

What would answer it

A study that measures it, and a reviewer to sign it off.

Last checked 2026-09-04. Searched: The sources listed in the receipts at the foot of this page.

Mechanism not reviewed

No reviewed mechanism story exists for this substance.

Why it matters. Recorded by the evidence model as a gap on this record.

What would answer it

A study that measures it, and a reviewer to sign it off.

Last checked 2026-09-04. Searched: The sources listed in the receipts at the foot of this page.

What happened in peopleRead from sources, not yet reviewed

Check any of this yourself

Every line above traced back to the study it came from. This is the technical layer, and the vocabulary changes here.

How many documents were read

  • 7 documents were read for this substance.

    RNAWiki source record

  • 7 of them state the same halfLife, and they agree.

    RNAWiki source record

  • 7 of them state the same volumeOfDistribution, and they agree.

    RNAWiki source record

Where else this substance is registered

FDA substance identifier (UNII)
762RDY0Y2H
RxNorm concept
486419

Checks this page had to pass

  • Passed

    Identity resolved

    no open identity hold

  • Passed

    No unresolved merge across substance families

    no quarantine open

  • Passed

    Every public sentence names a source

    The opening statement carries the origin: Written into the record, not signed off.

  • Not passed

    Trial roles classified for highlighted evidence

    No registered study is classified as testing this substance.

  • Passed

    No internal keys in reader text

    enforced by the copy-contract test over the rendered page

  • Passed

    Safety mode resolved

    Suppression classes recorded: S1, S3, S4.

  • Passed

    Canonical metadata present

    slug and display name present

What is missing or unclearRead from sources, not yet reviewed

How this medicine reached us

Kept near the foot of the page. A historical event moves up only when it changes something about this substance today.

What the approval register records

  • 14 approved applications cover products containing this substance. The earliest was NDA021673, approved 20041228 to GENZYME.

    Drugs@FDA application register · NDA021673 · read 2026-08-29

  • Marketing status on the register: discontinued, none (tentative approval) and prescription.

    Drugs@FDA application register · NDA021673 · read 2026-08-29

  • The earliest marketing start date recorded for a listed product is 20110901.

    FDA National Drug Code directory · 62756-030 · read 2026-08-29

What is missing or unclearRead from sources, not yet reviewed

What to learn next

Ordered by what would most change how you read this page, starting with what is easiest to misunderstand.

This order is fixed in code and does not count clicks or time on the page.

What is not here

9 questions this page could not answer

These sections were prepared and left out because there was nothing to put in them. They are listed rather than hidden, so the gaps in this record are visible.

  • What was measured, goal by goal — found nothing in the sources checked.
  • How close this is to real life — found nothing in the sources checked.
  • The path through the body — found nothing in the sources checked.
  • Felt, measured, or meaningful — found nothing in the sources checked.
  • How long anything takes — found nothing in the sources checked.
  • What it may clash with — found nothing in the sources checked.
  • Other ways to the same goal — found nothing in the sources checked.
  • Claims that go past the evidence — found nothing in the sources checked.
  • What changed on this page — found nothing in the sources checked.

The record as stored

The full record, for auditing

Everything above is built from what is below. This layer keeps the technical vocabulary, record identifiers and every stored row, so a reader who wants to check the page can.

Recorded evidence blocks (10)

On the Clofarabine label: indicated for what?


"Clofarabine injection is indicated for the treatment of pediatric patients 1 to 21 years old with relapsed or refractory acute lymphoblastic leukemia after at least two prior regimens. Clofarabine injection is a nucleoside metabolic inhibitor indicated for the treatment of pediatric patients 1 to 21 years old with…": indications and usage on Clofarabine's label. DailyMed label · 0da6764d-5fac-7e0f-ea3e-a5aee55a8b2d · 2024-02-27

149 registered trials of Clofarabine — at which phases?


Registered studies posting no result
75 of 149

149 registered studies of Clofarabine: 103 phase2, 66 phase1, 9 phase3, 1 na, 1 na or unstated. CLINICALTRIALS_SNAPSHOT · 2026-09-01

128 with a PubMed record

Show the evidence
  • phase2
    103
  • phase1
    66
  • phase3
    9
  • na
    1
  • na or unstated
    1
  • completed
    96
6 more recorded rows
  • terminated
    34
  • recruiting
    8
  • withdrawn
    5
  • active not recruiting
    3
  • unknown
    2
  • not yet recruiting
    1

recorded 2026-09-01 · last checked 2026-09-04

35 of Clofarabine's trials stopped: safety, futility/efficacy, accrual/recruitment, funding/business, sponsor decision unspecified, other?


safety (2), futility/efficacy (1), accrual/recruitment (17), funding/business (4), sponsor decision unspecified (3) and other (8): Clofarabine's stop wording, clustered. CLINICALTRIALS_SNAPSHOT · 2026-09-01

"low accrual"; 35 of 149 registered studies

Show the evidence

Trial

  • NCT00081887
    terminated; "low accrual"
  • NCT00241371
    terminated; "No response seen in patients"
  • NCT00503880
    terminated; "Genzyme discontinued Funding"
  • NCT00577694
    terminated; "funding unavailable"
  • NCT00593645
    terminated; "toxicities were worse than expected"
  • NCT00617929
    terminated; "Replaced by another protocol"
14 further recorded trials
  • NCT00626626
    terminated; "Investigator decision"
  • NCT00691652
    terminated; "Funding ended when only one subject enrolled and subject withdrew early."
  • NCT00700011
    terminated; "poor accrual"
  • NCT00708721
    terminated; "Data analysis revealed sufficient data for safety and efficacy"
  • NCT00750334
    terminated; "Terminated to focus on comparable trial, CLOMDS02507"
  • NCT00800566
    withdrawn; "Sponsor terminated."
  • NCT00814164
    terminated; "Sponsor withdrew support"
  • NCT00852709
    terminated; "Lack of accrual"
  • NCT00882076
    terminated; "study closed prematurely"
  • NCT00939653
    terminated; "Due to insufficient research institution participation and patient enrollment"
  • NCT00983528
    terminated; "Support withdrawn due to slow accrual"
  • NCT01003678
    terminated; "Drug provider withdrew support"
  • NCT01065545
    withdrawn; "Due to funding issues."
  • NCT01158885
    terminated; "Study terminated for lack of accrual."

recorded 2026-09-01 · last checked 2026-09-04

Human studies of Clofarabine used Clofarabine 40mg/m^2 — over how long?


studies of Clofarabine used the recorded amount. ClinicalTrials.gov · 2026-09-01

2 recorded entries; human; also "Clofarabine 40mg/m^2", "Clofarabine 22.5mg/m^2"

Show the evidence

human

  • NCT00067028
    Clofarabine 40mg/m^2
  • NCT00067028
    Clofarabine 22.5mg/m^2

recorded 2026-09-01 · last checked 2026-09-04

Clofarabine's half-life is 5.2 hours — which schedules were studied?


5.2 hours, the half-life Clofarabine's label states: "The terminal half-life was 5.2 hours." DailyMed label · 0da6764d-5fac-7e0f-ea3e-a5aee55a8b2d · 2024-02-27

Show the evidence
  • half life pharmacokinetics
    5.2 hours; The terminal half-life was 5.2 hours.
  • metabolism pharmacokinetics
    In vitr o studies using isolated human hepatocytes indicate very limited metabolism (0.2%).

recorded 2024-02-27 · last checked 2026-09-04

Which running trial of Clofarabine could settle lifespan?


NCT01885689 measures Progression-free Survival at 2 Years, reading out 2026-09-21.

5 open trials; n 72; "Clofarabine and Melphalan Before Donor Stem Cell Transplant in Treating Patients With Myelodysplasia, Acute Leukemia in Remission, or Chronic Myelomonocytic Leukemia"

Show the evidence

Trial

  • NCT01885689
    "Clofarabine and Melphalan Before Donor Stem Cell Transplant in Treating Patients With Myelodysplasia, Acute Leukemia in Remission, or Chronic Myelomonocytic Leukemia"; n 72; "Progression-free Survival at 2 Years"; 2026-09-21
  • NCT04644016
    "Cord Blood Transplant in Children and Young Adults With Blood Cancers and Non-malignant Disorders"; n 31; "Treatment related mortality at 1 year after myeloablative cord transplant"; 2026-12-20
  • NCT02727803
    "Personalized NK Cell Therapy in CBT"; n 100; "Progression free survival (PFS) time in C2C2 patients"; 2027-05-31
  • NCT03117751
    "Total Therapy XVII for Newly Diagnosed Patients With Acute Lymphoblastic Leukemia and Lymphoma"; n 790; "Event-free survival of ALL patients (EFS)"; 2028-09-30
  • NCT07566377
    "Cord Blood Transplantation in Children and Young Adults With Blood Cancer"; n 71; "Disease-free Survival (DFS)"; 2030-04-28

Which 42 trials of Clofarabine posted no result?


Posted no result
42 of 42 completed trials
Registrations
NCT00044889, NCT00028418, NCT00042354, NCT00098033, NCT00042341 and NCT00125827, and 36 more
Completion dates
oldest 2003-03; newest 2023-11
Show the evidence

Trial

  • NCT00044889
    2003-03
  • NCT00028418
    2004-03
  • NCT00042354
    2004-08
  • NCT00098033
    2005-09
  • NCT00042341
    2006-01
  • NCT00125827
    2006-02
14 further recorded trials
  • NCT00065143
    2006-02-22
  • NCT00201669
    2006-06
  • NCT00930098
    2007-07
  • NCT00125840
    2007-08
  • NCT01385891
    2010-02
  • NCT00477542
    2010-11
  • NCT00477945
    2010-11
  • NCT00641030
    2011-01
  • NCT00338494
    2011-04
  • NCT00991133
    2011-04
  • NCT01090167
    2011-04
  • NCT01196013
    2011-05
  • NCT00081822
    2011-08
  • NCT02544789
    2012-05

At the median, Clofarabine's trials enrolled 33.5 people — anything larger?


Median enrolment
33.5
Largest enrolment
5949
Registered trials counted
148

What do 1028 spontaneous reports say about Clofarabine — and not say?


These are reports people sent to a regulator. They do not show the medicine caused the reaction. Nobody counted how many people took the medicine and reported nothing. The same event can be reported more than once, and many reports are incomplete. News coverage, lawsuits and new warnings change how often people report. A count is not a rate and not a risk.

Clofarabine appears in spontaneous reports to regulators. Across the 10 most-reported reaction terms, 1028 reaction mentions were counted: febrile neutropenia 185; pyrexia 161; neutropenia 103; alanine aminotransferase increased 100. FAERS via Open Targets · CHEMBL1750 · 2026-06-24

Show the evidence
  • febrile neutropenia
    185
  • pyrexia
    161
  • neutropenia
    103
  • alanine aminotransferase increased
    100
  • aspartate aminotransferase increased
    95
  • vomiting
    87
4 more recorded rows
  • mucosal inflammation
    85
  • thrombocytopenia
    79
  • blood bilirubin increased
    68
  • pancytopenia
    65

recorded 2026-06-24 · last checked 2026-09-04

Which 10 reactions does Clofarabine's label not list?


alanine aminotransferase increased, aspartate aminotransferase increased and blood bilirubin increased and 7 more reported for Clofarabine, absent from its label. FAERS via Open Targets · CHEMBL1750 · 2026-06-24

2 label terms; 10 reported and unlisted; 0da6764d-5fac-7e0f-ea3e-a5aee55a8b2d

Show the evidence
  • alanine aminotransferase increased
    count not stated
  • aspartate aminotransferase increased
    count not stated
  • blood bilirubin increased
    count not stated
  • febrile neutropenia
    count not stated
  • mucosal inflammation
    count not stated
  • neutropenia
    count not stated
4 more recorded rows
  • pancytopenia
    count not stated
  • pyrexia
    count not stated
  • thrombocytopenia
    count not stated
  • vomiting
    count not stated

recorded 2026-06-24 · last checked 2026-09-04

Where it is registered
Identifiers, relations and other names

The exact record

ChEMBL id
CHEMBL1750
PubChem CID
119182
CAS number
123318-82-1
RxCUI
44151
InChIKey
WDDPHFBMKLOVOX-AYQXTPAHSA-N
Also called
Clofarabina, 18f-clofarabine, clo, 2-CHLORO-9-(2-DEOXY-2-FLUORO-.BETA.-D-ARABINOFURANOSYL)-9H-PURIN-6-AMINE, 9H-PURIN-6-AMINE, 2-CHLORO-9-(2-DEOXY-2-FLUORO-.BETA.-D-ARABINOFURANOSYL), CLOFARABINE [EMA EPAR], CLOFARABINE [JAN], CLOFARABINE [MART.], CLOFARABINE [MI], CLOFARABINE [ORANGE BOOK], CLOFARABINE [USAN], CLOFARABINE [VANDF]
Trade name
Clolar, Evoltra, Ivozall
Development code
NSC-759857
Sources (6)

Sources

ChEMBL 37 — CC BY-SA 3.0 Unported · ChEMBL ATC CC BY-SA · ClinicalTrials.gov — US Government work · Open Targets 26.06 — CC0 · mixed register set; per-register licences in docs/specs/corpus-20k-sources.md · openFDA / DailyMed — US Government work

How these records are assembled · Which registers were checked

Index-quality checks
  • identity passed: no open identity hold
  • required summary fields resolved: 4 required field(s) not terminal: Why people use it, Best-supported result, Biggest unanswered question, Human evidence
  • public claims reviewed: 0 reviewed claim(s); drafts are never rendered
  • source coverage passed: 6 source rows
  • no critical contamination: no quarantine open
  • canonical metadata passed: slug and display name present
  • no raw internal fields: enforced by the copy-contract test over the rendered page

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